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Quince Therapeutics doses first subject in Ataxia-Telangiectasia trial
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EryDex
Quince Therapeutics
ChromaDex wins orphan designation for rare ataxia drug
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EryDex
Nicotinamide Riboside
ChromaDex
FDA
Nanopore Long-Read Sequencing Facilitates Diagnosis of Atypical Ataxia-Telangiectasia
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Korea
late onset variant
Nanopore
Neurology Genetics
IBEC and AEFAT join forces against ataxia telangiectasia
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Spain
AEFAT
IBEC
Organoids to study ataxia telangiectasia
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Spain
IBEC
organoids
Boston Children's Hospital lab trying to develop drug to treat boy's deadly rare disease
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ASO
U.S. FDA Partial Clinical Hold Lifted on IND for EryDel’s Lead Phase 3 Asset EryDex for the Treatment of Ataxia-Telangiectasia
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EryDex
FDA
Quince Therapeutics
Governor of Queensland Celebrates Ataxia Telangiectasia Clinical Trial
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Australia
Triheptanoin
Acasti reports results from ataxia telangiectasia therapy trial
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GTX-102
Acasti Pharma
A New Model for Neurodegenerative Disease
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pig model
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